Efficient Prime Editing of Human Hematopoietic Stem Cells Corrects the Recurrent SBDS c.258+2T˃C Mutation and Recovers Engraftment Potential in Shwachman-Diamond Syndrome

제목
Efficient Prime Editing of Human Hematopoietic Stem Cells Corrects the Recurrent SBDS c.258+2T˃C Mutation and Recovers Engraftment Potential in Shwachman-Diamond Syndrome
저자
황규호
발행일
2025-11-21
학회명
Asian Transplantation Week 2025