Efficient prime editing of human hematopoietic stem cells corrects the recurrent SBDS c.258+2T˃C mutation and recovers engraftment potential in Shwachman-Diamond syndrome

제목
Efficient prime editing of human hematopoietic stem cells corrects the recurrent SBDS c.258+2T˃C mutation and recovers engraftment potential in Shwachman-Diamond syndrome
저자
황규호
발행일
2025-12-08
학회명
67th ASH® Annual Meeting and Exposition
개최지
미국 플로리다