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CRISPR/Cas9 PIG-A gene editing in nonhuman primate model demonstrates no intrinsic clonal expansion of PNH HSPCs
- Shin, Tae-Hoon;
- Baek, Eun Jung;
- Corat, Marcus A. F.;
- Chen, Shirley;
- Metais, Jean-Yves;
- 외 5명
Citations
WEB OF SCIENCE
19Citations
SCOPUS
21키워드
PAROXYSMAL-NOCTURNAL HEMOGLOBINURIA; HEMATOPOIETIC STEM; CELLS; MUTATIONS; PHENOTYPE
- 제목
- CRISPR/Cas9 PIG-A gene editing in nonhuman primate model demonstrates no intrinsic clonal expansion of PNH HSPCs
- 저자
- Shin, Tae-Hoon; Baek, Eun Jung; Corat, Marcus A. F.; Chen, Shirley; Metais, Jean-Yves; AlJanahi, Aisha A.; Zhou, Yifan; Donahue, Robert E.; Yu, Kyung-Rok; Dunbar, Cynthia E.
- 발행일
- 2019-06
- 유형
- Article
- 저널명
- Blood
- 권
- 133
- 호
- 23
- 페이지
- 2542 ~ 2545